
Mitochon Pharmaceuticals, Inc.Pennsylvania, United States

Solid Biosciences, Inc.Massachusetts, United States

Epirium Bio, Inc.California, United States

Synthena AGBern, Switzerland

Myostin Therapeutics Pty Ltd.Australia

Tarix Orphan LLCMA, US

PTC Therapeutics, Inc.New Jersey, United States

Italfarmaco SpA

ReveraGen BioPharma, Inc.United States

Akashi Therapeutics IncMassachusetts, United States